Write a properly referenced report on a human clinical trial using either a stem cell or a gene therapy (ie ATMP).Clinical efficacy of gene-modified stem cells in adenosine deaminase-deficient immunodeficiency.
https:/Avww. ncbi.nim.nih.gov/pubmed/28346229?dopt=Abstract
https://clinicattrials. gov/ct2/show/NCT00794508
Describe:
-disease to be treated and quality of life for patients,
-Current standard of care,
-what the tested therapy is and the rationale for use,
-any reported preclinical studies.
-how product was manufacturing and tested at release,
-Clinical tral details,
-overall findings of the trial